Capricor Therapeutics Showcases Long-Term Data at Global Congress

Capricor Therapeutics Highlights Long-Term Deramiocel Data

Capricor Therapeutics, Inc. (NASDAQ: CAPR), based in San Diego, is a biotechnology innovator that focuses on developing groundbreaking cell and exosome-based therapies aimed at addressing rare diseases. Recently, the company announced its plans to unveil pivotal three-year safety and efficacy results from its HOPE-2 open-label extension (OLE) study. This compelling data, showcasing the potential of deramiocel for treating Duchenne muscular dystrophy (DMD), will be presented during a late-breaking poster session at the upcoming World Muscle Society (WMS) Congress.

Exciting Developments for Deramiocel

The presentation is scheduled for the 29th Annual Congress of the World Muscle Society, taking place in Prague. Specifically, the findings will be shared during the session on October 11, focusing on the multi-modal benefits of deramiocel, also known as CAP-1002, in late-stage DMD patients. This innovative investigational therapy is designed to target both skeletal and cardiac muscle pathogenesis inherent in DMD.

Key Insights from HOPE-2 Study

According to Dr. Linda Marbán, CEO of Capricor, the new data from the HOPE-2 OLE trial marks a significant milestone. She expressed eagerness to share the outcomes, which they believe are crucial for advancing their Biologics License Application (BLA) for deramiocel's use in treating DMD-associated cardiomyopathy. These results not only substantiate the long-term impact of deramiocel but also underscore its relevance in the broader context of DMD treatment.

Details on the Poster Presentation

The poster presentation is titled "Multi-modal benefits of deramiocel (CAP-1002) in late-stage patients with DMD: a new treatment approach to target skeletal and cardiac muscle pathogenesis". Dr. Craig McDonald from UC Davis serves as the lead author, which highlights the robust research backing this innovative therapy.

About Capricor Therapeutics and Its Innovations

Capricor Therapeutics has distinguished itself with its commitment to pioneering cell and exosome therapies. Its lead therapeutic candidate, deramiocel, has shown promising results through various phases of clinical trials. These trials highlight its immunomodulatory and regenerative properties that have the potential to significantly affect patients with dystrophinopathies and heart diseases.

Advances in Exosome Technology

In addition to deramiocel, Capricor is also leveraging its proprietary StealthX™ exosome platform. This technology aims to facilitate the targeted delivery of therapeutics, which may transform the landscape for treating a range of complex diseases, from cancer to heart conditions. The company is actively focused on both clinical and preclinical developments, supporting a diverse array of applications.

Future Aspirations for Capricor

Capricor Therapeutics is not just looking at the present; it is committed to future research and development that holds the potential to change the lives of patients facing rare diseases. Their innovative approach seeks to address unmet medical needs, offering hope through scientifically validated therapies. This journey resonates with a mission to push the boundaries of what is possible in treatment options available for those afflicted with rare conditions.

Frequently Asked Questions

What data will Capricor present at the World Muscle Society Congress?

Capricor will present three-year safety and efficacy results from its HOPE-2 open-label extension study regarding deramiocel for treating Duchenne muscular dystrophy.

When is the poster presentation scheduled?

The presentation is set for October 11, during the World Muscle Society Congress in Prague.

What is deramiocel (CAP-1002)?

Deramiocel is an investigational therapy developed by Capricor that employs cardiac-derived cell therapy to target complications associated with Duchenne muscular dystrophy.

Who is the lead author of the poster presentation?

Dr. Craig McDonald from UC Davis will serve as the lead author of the presentation.

How does Capricor's exosome technology work?

Capricor's exosome technology, utilizing the StealthX™ platform, aims to facilitate targeted delivery of therapies to effectively address various diseases.

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