Amicus Therapeutics Announces Presentations and Posters at

New Post Public Reply Private Reply Replies (0) Message Board
News Desk 2018
Amicus Therapeutics Announces Presentations and Posters at Lysosomal Disease Network WORLD Symposium

CRANBURY, N.J., Jan. 26, 2015 (GLOBE NEWSWIRE) -- Amicus Therapeutics (Nasdaq: FOLD ), a biopharmaceutical company at the forefront of rare and orphan diseases, today announced that 2 oral presentations and 6 posters highlighting its development programs for lysosomal storage diseases will be included at the 11 th Annual Lysosomal Disease Network WORLD Symposium ( LDN WORLD ), to be held February 9-13, 2015 in Orlando, FL.

Oral Platform Presentations :

Fabry Disease :

  • Long-Term Efficacy and Safety of Migalastat Compared to Enzyme Replacement Therapy in Fabry Disease: Phase 3 Study Results – Derralynn Hughes, DPhil, University College London (Thursday, February 12 at 9:45 a.m. ET)

Pompe Disease :

  • Novel Recombinant Human Acid Alpha-Glucosidase with Optimal Glycosylation is Significantly Better than Standard of Care Enzyme Replacement for Glycogen Clearance in Skeletal Muscles of Gaa Knock-out Mice. – Russell Gotschall, Amicus Therapeutics, Inc. (Tuesday, February 10 at 4:15 p.m. ET)

Posters: Tuesday, February 10 - Thursday, February 12, 4:30-6:30 p.m. ET

Fabry Disease :

  • Long-Term Efficacy and Safety of Migalastat Compared to Enzyme Replacement Therapy in Fabry Disease: Phase 3 Study Results – Derralynn Hughes, DPhil, University College London (Poster #115)
  • Migalastat Reduces Left Ventricular Mass Index in Fabry Patients Naïve to ERT and Previously Treated with ERT – Daniel Bichet, M.D., M.Sc., University of Montreal (Poster #LB-2 – Late Breaker)
  • Improvement in Gastrointestinal Symptoms Observed in the Phase 3 FACETS Study of Migalastat in Fabry Patients – Raphael Schiffmann, M.D., M.H.Sc., Baylor University (Poster #230)
  • Accurate Quantitation of Plasma Globotriaosylsphingosine (lyso-Gb3) in Normal Individuals and Fabry Patients by Liquid Chromatography-Tandem Mass Spectrometry (LC-MS/MS) – Rick Hamler, Amicus Therapeutics, Inc. (Poster #100)

Pompe Disease :

  • Novel Recombinant Human Acid Alpha-Glucosidase with Optimal Glycosylation is Significantly Better than Standard of Care Enzyme Replacement for Glycogen Clearance in Skeletal Muscles of Gaa Knock-out Mice. – Russell Gotschall, Amicus Therapeutics, Inc. (Poster #94)
  • Histological Examination of the Effect of a Highly Phosphorylated Proprietary Recombinant Human Acid Alpha-Glucosidase on Glycogen Reduction in Disease-Relevant Muscles of Pompe Mice – Yi Lun, Amicus Therapeutics, Inc. (Poster #162)

About Amicus Therapeutics

Amicus Therapeutics (Nasdaq: FOLD ) is a biopharmaceutical company at the forefront of therapies for rare and orphan diseases. The Company is developing novel, first-in-class treatments for a broad range of human genetic diseases, with a focus on delivering new benefits to individuals with lysosomal storage diseases. Amicus' lead programs in development include the small molecule pharmacological chaperone migalastat as a monotherapy for Fabry disease, as well as next-generation enzyme replacement therapy (ERT) products for Fabry disease, Pompe disease, and MPS-1.

FOLD–G

Investors/Media: Amicus Therapeutics Sara Pellegrino Director, Investor Relations (609) 662-5044 Media: Pure Communications Dan Budwick (973) 271-6085

Scroll down for more posts ▼

Top 10 Most Recent News Articles

Pizza: The Unlikely Symbol of Universal Togetherness

Updated Category News Views 5

Why Pizza Is More Than Just Food They say a slice of pizza can tell a story. Whether it's a late-night snack amongst college buddies or the centerpiece of a family's Friday tradition, pizza unites like few others can. It morphs from a study aid into a tool for togetherness without skipping a beat, much like a chameleon of the food world. And no one understands this better...

Continue Reading
Larry Ellison's Moves Signal Confidence in Oracle's Future

Updated Category News Views 6

Unraveling Ellison's Bold Decision There's nothing like a sudden shift from a tech titan to make Wall Street sit up and take notice. Today, we got the word that Larry Ellison, Oracle's big gun as Executive Chair and CTO, has pulled the plug on his plan to sell Oracle stock. No dice, no distance covered under that plan. And he's made it crystal clear—selling isn't on his...

Continue Reading
Delhi Pushes Innovation Against Dryland Challenges

Updated Category News Views 5

Evolution of South-South Agricultural Cooperation Let's just say if there's a time to shine a spotlight on the arid lands of our world, it's now. The Global Drylands Congress 2026 in New Delhi put a sharp focus on scaling agricultural innovation across these thirsty regions. With climate change breathing down our necks, talking shop about food security isn't just for show...

Continue Reading
Silk Road Maritime Extends Its Global Reach in 2026

Updated Category News Views 5

China-Europe Trade Ties Continue to Tighten You ever watch a cargo ship glide into port and think, "There's a piece of the future right there”? Well, that's the scene at Poland’s Gdansk Port, now officially etched into the Silk Road Maritime route. This ain't just a couple of extra boats cutting through choppy waters—it's a great leap forward for a strained global...

Continue Reading
SystImmune's Data on Iza-bren Show Promise for Lung Cancer

Updated Category News Views 9

Stepping into New Territory with SystImmune Amid the cacophony of biotech whispers and the marketplace hum, SystImmune is trotting out something that might just make the folks in lab coats raise an eyebrow. They’ve got new data for Iza-bren—none of that flashy PR chatter—but it's damn promising if you ask me. At the World Conference on Lung Cancer in Seoul,...

Continue Reading
USPS Honors 150 Years of the U.S. Coast Guard Academy

Updated Category News Views 7

Honoring Tradition and Service The good ol’ U.S. Postal Service is at it again, giving a tip of the hat to a slice of American military heritage. This time, they’re putting out a new stamp to celebrate the 150th anniversary of the U.S. Coast Guard Academy. And you know where they did the honors? Right there on Custom House Pier in New London, Connecticut, a place that...

Continue Reading
Damp or Dry: The Battle for Healthy Air in Colorado

Updated Category News Views 4

The Hidden Cost of Colorado's Dry Air Dry climate isn't just a seasonal inconvenience—it's a real hidden cost to living comfortably and healthily in Colorado. With winters colder than a brass monkey's tail and summers that don't offer much relief in terms of humidity, your home's air quality is on the front line. So, what's the financial tale here, and how do you come...

Continue Reading
OneOdio Showcases Innovation at IFA 2026 in Berlin

Updated Category News Views 4

Echoes from Berlin IFA 2026 in Berlin was a cacophony of innovation, as OneOdio wrapped up its showcase with a bang. Boasting interactive activities and live DJ sets, the event echoed OneOdio's drive to meld advanced audio technology with the pulsating needs of music pros and everyday listeners. You couldn’t miss the excitement in the air at Booth 217. Tech Unplugged:...

Continue Reading
PathoSearch: A New Era in Pathology With Visual Search

Updated Category News Views 8

Revolutionizing Pathology with a Visual Search Engine In an era where time is money and precision is paramount, Aignostics is betting big on transforming the pathology landscape. Today, their announcement of PathoSearch, a visual search engine designed for retrieving comparable diagnosed pathology cases, marks a massive leap towards streamlining the diagnostic process....

Continue Reading
Protecting Teeth: Insights from Endodontist Dr. Joubert

Updated Category News Views 4

Preserving Our Natural Chompers Digging into the details of endodontic care, you realize how it's the unsung hero in the dental world. And let's face it, teeth don't get happier on their own when there's a problem on the inside. Dr. Christopher Joubert, a wiz on the endodontic front, spills the beans over at HelloNation about how essential these practices are in keeping...

Continue Reading

Top 5 Most Recently Viewed Articles

Compass Diversified Holdings Faces Class Action Lawsuit

Updated Category News Views 200

Compass Diversified Holdings Class Action Overview Pomerantz LLP has announced the initiation of a class action lawsuit against Compass Diversified Holdings (CODI or the Company) for concerns surrounding securities fraud and unlawful business practices. Investors who have experienced losses due to the company’s actions are urged to take note and consider joining the...

Continue Reading
ReShape Lifesciences and Vyome Therapeutics Merger Insights

Updated Category News Views 205

ReShape Lifesciences and Vyome Therapeutics Merger Insights ReShape Lifesciences Inc. (NASDAQ: RSLS), recognized for its innovative approach to weight loss and metabolic health solutions, has made significant strides in its merger agreement with Vyome Therapeutics, a clinical-stage company adept in immuno-inflammatory and rare diseases. This merger, rooted in a shared...

Continue Reading
Vantage Data Centers Secures Major €1.4B Investment Deal

Updated Category News Views 549

Vantage Data Centers Welcomes Significant Investment Vantage Data Centers, a premier global leader in hyperscale data center campuses, announces a remarkable investment agreement that is set to significantly enhance its EMEA data center platform. This groundbreaking deal, totalling €1.4 billion ($1.5 billion USD), will see investments from GIC, a respected global...

Continue Reading
DIVACS, Inc.: Innovating Value Management for Sales Success

Updated Category News Views 186

Introducing DIVACS, Inc. and Its Innovative Mission DIVACS, Inc. is proud to announce its launch as a revolutionary technology company that aims to change the way businesses handle value throughout the sales process and beyond. Founded by Ryan Schultz, DIVACS focuses on providing organizations with advanced tools and strategies geared toward enhancing sales performance...

Continue Reading
Tribe Property Technologies Enhances Community Management Efficiencies

Updated Category News Views 42

Enhancing Property Management with Innovative Features Tribe Property Technologies Inc. has recently made significant strides in enhancing its Tribe Home Community Platform. This platform introduces self-service features that simplify daily tasks for strata and condo communities, making life easier for residents while increasing efficiency for property managers and...

Continue Reading