Quote:

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For example, we have recently found a drug target and a potential drug for Wolfram syndrome. To bring this drug to our patients, we need to carry out dose-escalation studies and PK study, and design a clinical trial. We need to secure the intellectual property of our drug.

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http://wolframsyndrome.dom.wustl.edu/translat...-practice/

Is Dr. Urano referring to Dantrolene or the one of the other 4 out of 8 that are non FDA approved drugs.

http://wolframsyndrome.dom.wustl.edu/presenta...-uk-drugs/