Kylie O’Keefe Joins uniQure as Chief Customer and Strategy Officer
Introduction to Kylie O’Keefe's Role at uniQure
uniQure N.V. (NASDAQ: QURE), a leading gene therapy enterprise known for developing groundbreaking treatments for patients with critical medical needs, has announced an exciting new appointment. Kylie O’Keefe has joined the team as Chief Customer and Strategy Officer. She will play a pivotal role in the commercialization of AMT-130, an investigational gene therapy aimed at treating Huntington’s disease.
Professional Background of Kylie O’Keefe
Ms. O’Keefe brings a wealth of experience to uniQure, officially stepping into her new role on June 6, 2025. Previously, she was the Chief Commercial Officer at PTC Therapeutics, where she successfully developed and implemented global strategies for multiple rare neurology and metabolic products. With over 50 countries under her scope, her expertise lies in commercial launches and market strategy, which will be invaluable as uniQure anticipates a significant U.S. launch of AMT-130 in the near future.
Strategic Vision
“We are thrilled to welcome Kylie to our executive leadership as we prepare for the potential U.S. commercial launch of AMT-130 in 2026,” said Matt Kapusta, CEO of uniQure. He emphasized that O’Keefe’s extensive knowledge in rare diseases and her successful track record in gene therapy will greatly enhance uniQure’s strategic planning.
Significance of AMT-130
AMT-130 represents a revolutionary approach to treating Huntington’s disease, which has long needed an innovative solution. O’Keefe expressed her enthusiasm for joining uniQure at this critical juncture, stating, “AMT-130 has the potential to be the first disease-modifying treatment for Huntington’s disease.” This potential milestone highlights uniQure’s commitment to delivering transformative therapies.
Previous Experience and Education
Kylie O’Keefe’s extensive experience in the biopharmaceutical landscape includes significant roles at LEO Pharma, where she oversaw the launch of various pharmaceutical products globally. Her academic background complements her professional journey; she holds a Bachelor's degree in Biotechnology Innovation from Queensland University of Technology and a Graduate diploma in Managing Medical Product Innovation from Copenhagen Business School.
uniQure's Vision and Mission
uniQure's mission extends beyond launching AMT-130. The company is at the forefront of gene therapy, focusing on single treatments with potentially curative outcomes. Their success in pioneering therapies is showcased by their prior approval for hemophilia B, marking a historic achievement in genomic medicine. The company is also developing a pipeline of innovative therapies targeting several severe diseases, including ALS and Fabry disease.
Ongoing Commitment to Innovation
As uniQure navigates through this exciting phase, their commitment to advancing genetic therapies remains unwavering. The company ensures that every strategy and decision is aimed at meeting the urgent needs of patients suffering from rare diseases.
Conclusion
With Kylie O’Keefe's diverse background and strategic foresight, uniQure is poised to make significant advancements in the commercialization of AMT-130. Her leadership is expected to drive the company's mission to bridge the gap in the treatment landscape for Huntington’s disease and bring hope to affected patients.
Frequently Asked Questions
Who is Kylie O’Keefe?
Kylie O’Keefe is the newly appointed Chief Customer and Strategy Officer at uniQure, bringing extensive experience in the biopharmaceutical industry, particularly in rare diseases.
What is AMT-130?
AMT-130 is an investigational gene therapy developed by uniQure for the treatment of Huntington’s disease, aimed at modifying the disease's progression.
When is the expected launch of AMT-130?
The potential U.S. commercial launch of AMT-130 is anticipated around 2026, as part of uniQure's strategy to bring innovative treatments to market.
What is uniQure's mission?
uniQure is committed to advancing gene therapies that provide potentially curative outcomes for patients with severe medical conditions, emphasizing innovation in treatment approaches.
What other diseases is uniQure focusing on?
In addition to Huntington’s disease, uniQure is developing therapies for ALS, refractory temporal lobe epilepsy, and Fabry disease, enhancing their portfolio of critical treatments.
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